Definitions of terms and regulations

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There are currently 6 glossary in this directory beginning with the letter A.
Access to Treatment Committee
The Committee at n-Lorem that reviews proposals from physicians to treat genetically confirmed nano-rare disease patients.
A suspension of fine solid or liquid particles in gas. In medicine, aerosols can be used to administer drugs.
One of two or more alternative forms of a gene that arise by mutation and are found at the same place on a chromosome.
amino acids
The building blocks of proteins, consisting of organic compounds containing an amino group and a carboxyl group.
A chemical substance that is the subject of chemical analysis.
antisense oligonucleotides (ASOs)
Short, synthetic, single-stranded oligodeoxynucleotides that can alter RNA and reduce, restore or modify protein expression through several distinct mechanisms.

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