Commitment to Safety First: The DSMB
with Eugene Schneider, M.D.
Connor’s Story: A First for TUBB4A Treatment
with Diana and Mike Gooley
Connor Dalby’s Story: n-Lorem Patient #001
with Kelley Dalby and Dr. Olivia Kim-McManus
Our Mission is Personal
with Sarah Glass, Ph.D.
Rosie’s Story: A Nano-rare Treatment Pioneer
with Nicole and Bobby Glenn
Sloane’s Story: A Shared Medicine
with Megan Hedstrom and Tom Lowe
Susannah’s Progress: Two Years of ASO Treatment
with Dr. Jennifer Bain and Luke Rosen
Sneak Peek of the 2024 Nano-rare Patient Colloquium
Brady Huggett interviews Stan Crooke
The Building Blocks of What’s Possible
with David Butler, Ph.D.
