Seeing with Grace: A Teen’s Journey with a Rare Vision-Affecting Disease
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Sneak Peek of the 2025 Nano-rare Patient Colloquium
Brady Huggett interviews Stan Crooke
Meet Rescue 7: Firefighters Serving Patients
with Luke Rosen, Raena and Frank Vrtochnick
Hope for Kinsley: Facing TUBB4A with Courage and Care
with Sarah and Ryan Marta
Commitment to Safety First: The DSMB
with Eugene Schneider, M.D.
Connor’s Story: A First for TUBB4A Treatment
with Diana and Mike Gooley
Connor Dalby’s Story: n-Lorem Patient #001
with Kelley Dalby and Dr. Olivia Kim-McManus
Our Mission is Personal
with Sarah Glass, Ph.D.
Rosie’s Story: A Nano-rare Treatment Pioneer
with Nicole and Bobby Glenn
