n-Lorem Foundation Organizes Third Annual Nano-rare Patient Colloquium, Highlighting Scientific and Clinical Advancements Achieved Since Organization’s Founding
Hosted by Biogen, the [...]
Sneak Peek of the 2025 Nano-rare Patient Colloquium
Brady Huggett interviews Stan Crooke
Lesson 19 – How siRNAs and ASOs Differ
Lessons in Antisense [...]
Lesson 18 – The Limits of ASO Technology
Lessons in Antisense [...]
Meet Rescue 7: Firefighters Serving Patients
with Luke Rosen, Raena and Frank Vrtochnick
Restoration of GBE1 Protein Activity with an ASO: Impact of a Common Sequencing Error on Drug Discovery
Let’s Discuss Science [...]
n-Lorem Foundation Publishes Study Showing Targeted ASO Therapy Restores GBE1 Protein in APBD Patient Cells
Research, published in Nucleic [...]
Lesson 17 – The Science of ASO Design and Screening Using the FDA Guidance for Nano-rare Patients
Lessons in Antisense [...]
