Establishing a commercial solution for extremely rare genetic diseases
Crooke, S.T., Lo, A.W. Download PDF
A way forward for diagnosis of patients with extremely rare genetic mutations
Crooke, S.T., Kim-McManus, O.S., Dalby, K. Download PDF
A call to arms against ultra-rare diseases
Crooke, S.T. Download PDF
Ultra-precision medicine
Crooke, S.T. Download PDF
Chemical modification of PS-ASO therapeutics reduces cellular protein-binding and improves the therapeutic index
Shen, W., De Hoyos, C.L., Migawa, M.T., Vickers, T.A., Sun, H., Low, A., Bell, T.A. 3rd., Rahdar, M., Mukhopadhyay, S., Hart, C.E., Bell, M., Riney, S., Murray, S.F., Greenlee, S., Crooke, R.M., Liang, X.H., Seth, P.P., Crooke, S.T.
