BioMarin and n-Lorem Foundation Enter Early Research Collaboration to Develop Potential First-in-Disease Medicine for Newly Identified ReNU Syndrome
ReNU syndrome was discovered [...]
New Publication Provides an Unprecedented Look at the Largest Reported Cohort of Nano-Rare Patients Evaluated for Individualized ASO Therapies
First-of-its-kind perspective from the [...]
n-Lorem Foundation Announces the 50th Nano-rare Patient Receives Personalized ASO Medicine
Physicians collaborating with [...]
n-Lorem Publishes Commentary Offering Insight into Potential Commercialization Strategies for Nano-rare Medicines
The commentary titled ‘Establishing [...]
n-Lorem Foundation Publishes Study Showing Targeted ASO Therapy Restores GBE1 Protein in APBD Patient Cells
Research, published in Nucleic [...]
n-Lorem Foundation Celebrates Five Years of Bringing Hope and Potential Treatments to Nano-rare Patients
Demand from the nano-rare [...]
Multi-year Grant from National Institutes of Health URGenT Network Funds Treatment of Patients with Ultra-Rare CHCHD10-ALS
$15 million grant supports [...]
