Addressing the needs of nano-rare patients: the n-Lorem experience
Crooke, S.T., Glass, S., Gleeson, J.G., Mignon, L., Skourti-Stathaki, K., Douville, J., Knutsen, M., Pu, H., Bain, J.M., Berry-Kravis, E., Shneider, N.A., Kim-McManus, O., Eichler, F.S., Chung, W.K., Nagy, A., Kaufmann, H., Gonzalez-Duarte, A., Oskarsson, B., McCourt, E.A., Leung, N. Download PDF