Individualized antisense oligonucleotides for SCN2A-related developmental epileptic encephalopathy
Kim-McManus, O., Mignon, L., Douville, J., Pu, H., Parisien, C., Glass, S., Bennett, C.F., Celso, J., Robbins, K., Ung, H., Olson, H., Kingsmore, S.F., Petrou, S., Crooke, S.T., Gleeson, J.G., Berry-Kravis, E. Download PDF