A way forward for diagnosis of patients with extremely rare genetic mutations
Crooke, S.T., Kim-McManus, O.S., Dalby, K.
Personalized antisense oligonucleotides ‘for free, for life’ — the n-Lorem Foundation
Gleeson, J.G., Bennett, F.B., Carroll, J.B., Cole, T., Douville, J., Glass, S., Tekendo-Ngongang, C., Williford, A.C., Crooke, S.T.
Antisense Technology: A Review
Crooke, S.T., Liang, X.H., Baker, B.F., Crooke R.M.
Evaluating human mutation databases for ‘Treatability’ using personalized antisense oligonucleotides
Mittal, S., Tang, I., Gleeson, J.G.
Antisense oligonucleotide as a therapeutic approach in amyotrophic lateral sclerosis
Korobeynikov, V.A., Lyashchenko, A.K., Blanco-Redondo, B., Jafar-Nejad, P. Shneider, N.A.
IND Submissions for Individualized Antisense Oligonucleotide Drug Products for Severely Debilitating or Life-Threatening Diseases: Chemistry, Manufacturing, and Controls Recommendations
U.S. Department of Health and Human Services
Food and Drug Administration
Center for Drug Evaluation and Research (CDER)
Download PDF
Perinuclear positioning of endosomes can affect PS-ASO activities
Liang, X.H., Nichols, J.G., Tejera, D., Crooke, S.T.
IND Submissions for Individualized Antisense Oligonucleotide Drug Products for Severely Debilitating or Life-Threatening Diseases: Clinical Recommendations
U.S. Department of Health and Human Services
Food and Drug Administration
Center for Drug Evaluation and Research (CDER)
Download PDF
