Coming Together for the Nano-rare Patient
with Dr. John Maraganore
Antisense (How we do it at n-Lorem)
How we [...]
Anna’s Story of Hope and Help
with Dr. Neil Shneider and Sonja Kämpfer
Why ASO Technology?
What makes [...]
Advocating for Rare Patients
with Wendy Erler
Drug Discovery Platforms
There are [...]
Clinical Trials for One Patient
with Dr. Joe Gleeson
How Drugs are Used
Drugs are [...]
A Diagnostic Odyssey: The UDN and n-Lorem’s Roles
with Dr. Francis Sessions Cole, III
Susannah’s Story:
with Dr. Wendy Chung and Luke Rosen
