A bespoke genetic therapy is helping Susannah. Can similar drugs be made at scale for other rare diseases? [...] Andrew Andrew Serrano2024-08-13T21:17:30-04:00 Read More
A teenager faced constant seizures. Could a drug developed just for him stop them? [...] Andrew Andrew Serrano2024-07-17T22:25:21-04:00 Read More
ASOs Drive Foundation’s Work to Develop Treatments for the World’s Rarest Diseases [...] Andrew Andrew Serrano2024-07-17T23:25:10-04:00 Read More
This lifesaving treatment was designed for one. Could it be the future of medical care? [...] Andrew Andrew Serrano2023-11-27T20:53:46-04:00 Read More
n-Lorem Foundation Bringing Real Hope To ‘n-of-1’ Patients [...] Andrew Andrew Serrano2024-08-13T21:15:06-04:00 Read More
They Created a Drug for Susannah: What About Millions of Other Patients? [...] mikejaram2024-07-17T22:16:58-04:00 Read More
Baylor College of Medicine welcomes 10 new leaders to the Board of Advisors [...] mikejaram2023-02-02T02:49:06-04:00 Read More
New Silence ALS Initiative is Giving Hope to Nano-rare Patients [...] mikejaram2024-07-17T23:26:58-04:00 Read More
San Diego Biotech Nonprofit Providing Hope for Patients With Ultra-Rare Diseases [...] mikejaram2023-02-15T21:46:31-04:00 Read More
A Devastating Rare Disease Inspires a Medicine Created Just for her Son. Will it Work? [...] mikejaram2024-07-17T23:27:44-04:00 Read More
