n-Lorem Foundation Organizes Third Annual Nano-rare Patient Colloquium, Highlighting Scientific and Clinical Advancements Achieved Since Organization’s Founding
Hosted by Biogen, the [...]
n-Lorem Foundation Publishes Study Showing Targeted ASO Therapy Restores GBE1 Protein in APBD Patient Cells
Research, published in Nucleic [...]
n-Lorem Foundation Celebrates Five Years of Bringing Hope and Potential Treatments to Nano-rare Patients
Demand from the nano-rare [...]
Multi-year Grant from National Institutes of Health URGenT Network Funds Treatment of Patients with Ultra-Rare CHCHD10-ALS
$15 million grant supports [...]
GondolaBio and n-Lorem Foundation Partner to Advance Novel ASO Therapies for Genetic Diseases
Collaboration provides GondolaBio access [...]
n-Lorem Publishes Recommendations for Treating Patients with Heterozygous Toxic Gain of Function Mutations
Article published in Nucleic [...]
Positive Clinical Observations from n-Lorem Treated, KIF1A Nano-rare Patient Published in Nature Medicine
Case study, published in [...]
