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Pathwaymikejaram2022-11-09T06:45:52+00:00

Slide Step 1 Tertiary
care center

Step 2 Application for
Treatment is submitted
to n-Lorem

Physicians Patients Institutions Step 3 ATTC reviews
application

Step 4 n-Lorem reviews and makes a decision
Step 5 Patient consents and genome sequencing begins
Step 6 ASO discovery starts
Step 7 Natural history
collection begins

Step 8 ASO development and manufacturing begins
Step 12 Patient begins
treatment

Step 11 Step 10 Institution review board and master service agreements Sterile fill and finish (Occurs in tandem with Step 11)

Step 9 IND preparation and
filing begins

Duration:
(N/A)
Duration:
(N/A)
Duration:
(Ongoing from discovery to dosing)
Duration:
(3 months)
Duration:
(2 months)
Duration:
(1-3 months)
Duration:
(2 months)
Initiation to treatment:
(Steps 6-12)
15-18 months on avg.
Duration:
(7 months)
Duration:
(1-2 months)
Duration:
(N/A)
Duration:
(1-3 months)
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© n-Lorem Foundation. All rights reserved.
n-Lorem Foundation is a qualified 501(c)(3) tax-exempt organization. EIN: # 84-3288113
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