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Susannah Receives Personalized Medicine

December 19, 2022|Tags: |

Among the three patients treated this fall is Susannah, a beautiful 8 year old girl who suffers from a neurodegenerative nano-rare condition. Susannah is receiving a personalized, experimental ASO discovered and developed for her unique mutation.

3 minutes


Special Webinar on N of 1 | Access | Innovation co hosted by Biogen

April 30, 2021|Tags: |

36 minutes
RNA Targeted Drug Discovery: From Pipe Dream to Reality

April 19, 2021|Tags: |

We are continuously developing new partnerships, new treatments, and solutions to those with nano-rare diseases. Contact us to learn more about our organization.

We cannot do
this alone

Together we are changing the world—
one patient at a time

We hope that you join us on this journey to discover, develop and provide individualized antisense medicines for free for life for nano-rare patients. The ultimate personalized medicine approach – for free, for life.

We need your support

Join us on our Corps of Discovery of the mind and heart. Help us bring hope and potential help to nano-rare patients today. For free, for life.

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