Treatment Start Date:
March 2024
Video Timeline
Milestones
May 2024
Assisted Walk
Connor walks with the help of his mom, never being able to take more than a few steps on his own
June 2024
“He’s literally walking”
For the first time, Connor is able to walk a short distance unassisted
June 2024
Improved distance
Connor walks a significantly longer distance with improvement in balance
We cannot do
this alone
Together we are changing the world—
one patient at a time
We hope that you join us on this journey to discover, develop and provide individualized antisense medicines for free for life for nano-rare patients. The ultimate personalized medicine approach – for free, for life.
Nano-rare patients need your support
Having access to a potentially life-saving treatment can make all the difference in the world, but it takes all of us coming together to help nano-rare patients. Please support our work to bring hope and potential help to nano-rare patients today.
For free, for life.
For free, for life.
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