North Texas girl to become first patient to receive treatment for rare genetic disorder [...] Andrew Andrew Serrano2025-05-05T18:48:51-04:00 Read More
For the many and the few: bringing ASO therapies to both mainstream and nano-rare indications [...] Andrew Andrew Serrano2025-05-07T11:56:59-04:00 Read More
Parents, doctors, medical researchers seek treatment for disease with no name [...] Andrew Andrew Serrano2025-05-05T18:44:50-04:00 Read More
A bespoke genetic therapy is helping Susannah. Can similar drugs be made at scale for other rare diseases? [...] Andrew Andrew Serrano2024-08-13T21:17:30-04:00 Read More
