n-Lorem Foundation Celebrates Five Years of Bringing Hope and Potential Treatments to Nano-rare Patients
Demand from the nano-rare [...]
Lesson 1 – Introduction
Lessons in Antisense [...]
Nano-rare Patient Colloquium / 2025 – Lineup
October 20-21, 2025 - Cambridge, MA Join us for our annual Nano-rare patient Colloquium. This event is free to attend — register today!
Our Mission is Personal
with Sarah Glass, Ph.D.
n-Lorem: Celebrating 5 Years of Hope
3 minutes
A toxic gain-of-function variant in MAPK8IP3 provides insights into JIP3 cellular roles
Zhang, W., Mittal, S., Thomas, R., Foroughishafiei, A., Nunes Bastos, R., Chung, W., Skourti-Stathaki, K., Crooke, S.T.
Multi-year Grant from National Institutes of Health URGenT Network Funds Treatment of Patients with Ultra-Rare CHCHD10-ALS
$15 million grant supports [...]
