
Treatment Start Date:
October 2022
Susannah’s Story
Video Timeline
Milestones
Standing up
For the first time, Susannah is able to stand on her own. Proud of herself, she playfully teaches her father ‘how to stand up’.
Playing basketball
Testing her motor control skills, Sus shoots a basketball with her brother.
Climbing Stairs
Climbing stairs involves coordinated muscle activation in the legs, hips, and core to propel the body upwards step-by-step, while maintaining balance and proper weight distribution, making it a demanding activity that tests multiple aspects of neuromuscular function.

We cannot do
this alone
Together we are changing the world—
one patient at a time
We hope that you join us on this journey to discover, develop and provide individualized antisense medicines for free for life for nano-rare patients. The ultimate personalized medicine approach – for free, for life.
Follow us on social for updates on our latest efforts