Process

n-Lorem - Patient to Treatment Workflow

Upon regulatory permission of the ASO drug, an investigator-led clinical trial can then be initiated, in which individual patients will receive their custom ASO treatments.

The Foundation plans to provide ASO treatments to patients for the rest of their lives at cost. To help balance cost, the Foundation will work with the Regulatory authorities to gain approval for continuing use that would allow future treatment to be covered by the patients’ insurance.